Gene Therapy News and Research

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Gene therapy is an experimental technique that uses genes to treat or prevent disease. In the future, this technique may allow doctors to treat a disorder by inserting a gene into a patient’s cells instead of using drugs or surgery.
New gene therapy can protect visual function in patients with dominant optic atrophy

New gene therapy can protect visual function in patients with dominant optic atrophy

Researchers use metal-organic frameworks to target prostate cancer cells

Researchers use metal-organic frameworks to target prostate cancer cells

Researchers identify rare genetic marker that protects against cardiovascular disease

Researchers identify rare genetic marker that protects against cardiovascular disease

Somatic mutation acts as natural gene therapy in patients with GATA2 deficiency

Somatic mutation acts as natural gene therapy in patients with GATA2 deficiency

Light-activated liposomes could help deliver CRISPR gene therapy

Light-activated liposomes could help deliver CRISPR gene therapy

New approach can prevent toxicity linked to neurological gene therapy

New approach can prevent toxicity linked to neurological gene therapy

Dietary induction of hepatocyte regeneration could help enhance gene repair in the liver

Dietary induction of hepatocyte regeneration could help enhance gene repair in the liver

Research projects receive BTCA awards to develop new drugs

Research projects receive BTCA awards to develop new drugs

New DNA-cutting tool could advance gene editing for novel treatments

New DNA-cutting tool could advance gene editing for novel treatments

Immunotherapy using CAR NKT cells shows promise for treating solid tumors

Immunotherapy using CAR NKT cells shows promise for treating solid tumors

Newly developed biodegradable microneedles deliver genes into the skin

Newly developed biodegradable microneedles deliver genes into the skin

Microneedles For Therapeutic Gene Delivery

Microneedles For Therapeutic Gene Delivery

Researchers discover novel genes for human deafness in Israeli families

Researchers discover novel genes for human deafness in Israeli families

Gene therapy overcomes cardiac effects in mouse model of Freidreich’s ataxia

Gene therapy overcomes cardiac effects in mouse model of Freidreich’s ataxia

Researchers compare developed carriers for delivery of genome editing tools

Researchers compare developed carriers for delivery of genome editing tools

CRISPR in a Box: New educational gene editing tool kit

CRISPR in a Box: New educational gene editing tool kit

Researchers develop new gene therapy for congenital blindness

Researchers develop new gene therapy for congenital blindness

AF4-MALS: A powerful tool to separate viruses and aggregates

AF4-MALS: A powerful tool to separate viruses and aggregates

Study looks into safety and early outcomes of gene therapy for spinal muscular atrophy

Study looks into safety and early outcomes of gene therapy for spinal muscular atrophy

Eliminating tumors with engineered ‘off-the-shelf’ therapeutic T cells

Eliminating tumors with engineered ‘off-the-shelf’ therapeutic T cells