Gene Therapy News and Research

RSS
Gene therapy is an experimental technique that uses genes to treat or prevent disease. In the future, this technique may allow doctors to treat a disorder by inserting a gene into a patient’s cells instead of using drugs or surgery.
Study shows beneficial effects of gene therapy can be observed even after several decades

Study shows beneficial effects of gene therapy can be observed even after several decades

Study shows how human viruses are better adapted to infect certain tissues

Study shows how human viruses are better adapted to infect certain tissues

First-in-human clinical trial to test safety, efficacy of gene therapy for Alzheimer's disease

First-in-human clinical trial to test safety, efficacy of gene therapy for Alzheimer's disease

New understanding of tumor microenvironment could help enhance immunotherapy

New understanding of tumor microenvironment could help enhance immunotherapy

New AI-based method produces new diversity of AAV capsids for optimized gene therapy

New AI-based method produces new diversity of AAV capsids for optimized gene therapy

Severe genetic immunodeficiency reversed by a rare DNA change

Severe genetic immunodeficiency reversed by a rare DNA change

Gene therapy helps paralyzed mice to walk again

Gene therapy helps paralyzed mice to walk again

Innovative gene therapy approach for regeneration of functional new neurons

Innovative gene therapy approach for regeneration of functional new neurons

New gene therapy approach can improve uterine blood flow in placental insufficiency

New gene therapy approach can improve uterine blood flow in placental insufficiency

Gene therapy and medication can provide certain beneficial effects of physical exercise

Gene therapy and medication can provide certain beneficial effects of physical exercise

A Gene Mutation That Protects Against Disease

A Gene Mutation That Protects Against Disease

New gene therapy can protect visual function in patients with dominant optic atrophy

New gene therapy can protect visual function in patients with dominant optic atrophy

Researchers use metal-organic frameworks to target prostate cancer cells

Researchers use metal-organic frameworks to target prostate cancer cells

Researchers identify rare genetic marker that protects against cardiovascular disease

Researchers identify rare genetic marker that protects against cardiovascular disease

Somatic mutation acts as natural gene therapy in patients with GATA2 deficiency

Somatic mutation acts as natural gene therapy in patients with GATA2 deficiency

Light-activated liposomes could help deliver CRISPR gene therapy

Light-activated liposomes could help deliver CRISPR gene therapy

New approach can prevent toxicity linked to neurological gene therapy

New approach can prevent toxicity linked to neurological gene therapy

Dietary induction of hepatocyte regeneration could help enhance gene repair in the liver

Dietary induction of hepatocyte regeneration could help enhance gene repair in the liver

Research projects receive BTCA awards to develop new drugs

Research projects receive BTCA awards to develop new drugs

New DNA-cutting tool could advance gene editing for novel treatments

New DNA-cutting tool could advance gene editing for novel treatments